CaRLO — Cancer Research Library Online

1

AAV-9 mediated phosphatase-1 inhibitor-1 overexpression improves cardiac contractility in unchallenged mice but is deleterious in pressure-overload (2018)

D M Schwab; L Tilemann; R Bauer; M Heckmann; A Jungmann; M Wagner; J Burgis; C Vettel; H A Katus; A El-Armouche; O J Müller

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-01-20

Description: AAV-9 mediated phosphatase-1 inhibitor-1 overexpression improves cardiac contractility in unchallenged mice but is deleterious in pressure-overload AAV-9 mediated phosphatase-1 inhibitor-1 overexpression improves cardiac contractility in unchallenged mice but is deleterious in pressure-overload, Published online: 19 January 2018; doi:10.1038/gt.2017.97 AAV-9 mediated phosphatase-1 inhibitor-1 overexpression improves cardiac contractility in unchallenged mice but is deleterious in pressure-overload

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

2

Conditional replication of oncolytic viruses based on detection of oncogenic mRNA (2018)

M Renteln

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-01-20

Description: Conditional replication of oncolytic viruses based on detection of oncogenic mRNA Conditional replication of oncolytic viruses based on detection of oncogenic mRNA, Published online: 19 January 2018; doi:10.1038/gt.2017.99 Conditional replication of oncolytic viruses based on detection of oncogenic mRNA

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

3

CCAT1 stimulation of the symmetric division of NSCLC stem cells through activation of the Wnt signalling cascade (2018)

Chongwen Xu; Guodong Xiao; Boxiang Zhang; Meng Wang; Jichang Wang; Dapeng Liu; Jing Zhang; Hong Ren; Xin Sun

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-01-20

Description: CCAT1 stimulation of the symmetric division of NSCLC stem cells through activation of the Wnt signalling cascade CCAT1 stimulation of the symmetric division of NSCLC stem cells through activation of the Wnt signalling cascade, Published online: 19 January 2018; doi:10.1038/gt.2017.98 CCAT1 stimulation of the symmetric division of NSCLC stem cells through activation of the Wnt signalling cascade

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

4

Evaluation of the Glypican 3 promoter for transcriptional targeting of hepatocellular carcinoma (2018)

Bijay Dhungel; Slawomir Andrzejewski; Aparna Jayachandran; Ritu Shrestha; Charmaine A. Ramlogan-Steel; Christopher J. Layton; Jason C. Steel

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-03-22

Description: Evaluation of the Glypican 3 promoter for transcriptional targeting of hepatocellular carcinoma Evaluation of the Glypican 3 promoter for transcriptional targeting of hepatocellular carcinoma, Published online: 21 March 2018; doi:10.1038/s41434-018-0002-2 Evaluation of the Glypican 3 promoter for transcriptional targeting of hepatocellular carcinoma

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

5

HIV-based lentivirus-mediated vasoactive intestinal peptide gene delivery protects against DIO animal model of Type 2 diabetes (2018)

Hale M. Tasyurek; Yunus E. Eksi; Ahter D. Sanlioglu; Hasan A. Altunbas; Mustafa K. Balci; Thomas S. Griffith; Salih Sanlioglu

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-03-12

Description: HIV-based lentivirus-mediated vasoactive intestinal peptide gene delivery protects against DIO animal model of Type 2 diabetes HIV-based lentivirus-mediated vasoactive intestinal peptide gene delivery protects against DIO animal model of Type 2 diabetes, Published online: 09 March 2018; doi:10.1038/s41434-018-0011-1 HIV-based lentivirus-mediated vasoactive intestinal peptide gene delivery protects against DIO animal model of Type 2 diabetes

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

6

Improving therapeutic efficacy of IL-12 intratumoral gene electrotransfer through novel plasmid design and modified parameters (2018)

C. Burkart; A. Mukhopadhyay; S. A. Shirley; R. J. Connolly; J. H. Wright; A. Bahrami; J. S. Campbell; R. H. Pierce; D. A. Canton

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-03-12

Description: Improving therapeutic efficacy of IL-12 intratumoral gene electrotransfer through novel plasmid design and modified parameters Improving therapeutic efficacy of IL-12 intratumoral gene electrotransfer through novel plasmid design and modified parameters, Published online: 09 March 2018; doi:10.1038/s41434-018-0006-y Improving therapeutic efficacy of IL-12 intratumoral gene electrotransfer through novel plasmid design and modified parameters

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

7

In vivo selection with lentiviral expression of Bcl2 T69A/S70A/S87A mutant in hematopoietic stem cell-transplanted mice (2018)

Yan-Yi Wang; Shan Ma; Qingyong Chen; Demin Jiao; Yong Yang

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-03-12

Description: In vivo selection with lentiviral expression of Bcl2 T69A/S70A/S87A mutant in hematopoietic stem cell-transplanted mice In vivo selection with lentiviral expression of 〈i〉Bcl2〈/i〉〈sup〉 T69A/S70A/S87A 〈/sup〉 mutant in hematopoietic stem cell-transplanted mice, Published online: 09 March 2018; doi:10.1038/s41434-018-0008-9 In vivo selection with lentiviral expression of Bcl2 T69A/S70A/S87A mutant in hematopoietic stem cell-transplanted mice

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

8

Widespread transduction of astrocytes and neurons in the mouse central nervous system after systemic delivery of a self-complementary AAV-PHP.B vector (2018)

Melvin Y. Rincon; Filip de Vin; Sandra I. DuquéShelly Fripont; Stephanie A. Castaldo; Jessica Bouhuijzen-Wenger; Matthew G. Holt

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-03-12

Description: Widespread transduction of astrocytes and neurons in the mouse central nervous system after systemic delivery of a self-complementary AAV-PHP.B vector Widespread transduction of astrocytes and neurons in the mouse central nervous system after systemic delivery of a self-complementary AAV-PHP.B vector, Published online: 09 March 2018; doi:10.1038/s41434-018-0005-z Widespread transduction of astrocytes and neurons in the mouse central nervous system after systemic delivery of a self-complementary AAV-PHP.B vector

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

9

AAV1.NT-3 gene therapy increases muscle fiber diameter through activation of mTOR pathway and metabolic remodeling in a CMT mouse model (2018)

Mehmet E. Yalvac; Jakkrit Amornvit; Lei Chen; Kimberly M. Shontz; Sarah Lewis; Zarife Sahenk

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-03-12

Description: AAV1.NT-3 gene therapy increases muscle fiber diameter through activation of mTOR pathway and metabolic remodeling in a CMT mouse model AAV1.NT-3 gene therapy increases muscle fiber diameter through activation of mTOR pathway and metabolic remodeling in a CMT mouse model, Published online: 09 March 2018; doi:10.1038/s41434-018-0009-8 AAV1.NT-3 gene therapy increases muscle fiber diameter through activation of mTOR pathway and metabolic remodeling in a CMT mouse model

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

10

AAV-mediated NT-3 overexpression protects cochleae against noise-induced synaptopathy (2018)

Hengchao Chen; Yazhi Xing; Li Xia; Zhengnong Chen; Shankai Yin; Jian Wang

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-03-14

Description: AAV-mediated NT-3 overexpression protects cochleae against noise-induced synaptopathy AAV-mediated NT-3 overexpression protects cochleae against noise-induced synaptopathy, Published online: 13 March 2018; doi:10.1038/s41434-018-0012-0 AAV-mediated NT-3 overexpression protects cochleae against noise-induced synaptopathy

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

11

MR-guided delivery of AAV2-BDNF into the entorhinal cortex of non-human primates (2018)

Alan H. Nagahara; Bayard R. Wilson; Iryna Ivasyk; Imre Kovacs; Saytam Rawalji; John R. Bringas; Phillip J. Pivirotto; Waldy San Sebastian; Lluis Samaranch; Krystof S. Bankiewicz; Mark H. Tuszynski

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-03-14

Description: MR-guided delivery of AAV2-BDNF into the entorhinal cortex of non-human primates MR-guided delivery of AAV2-BDNF into the entorhinal cortex of non-human primates, Published online: 13 March 2018; doi:10.1038/s41434-018-0010-2 MR-guided delivery of AAV2-BDNF into the entorhinal cortex of non-human primates

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

12

Understanding the molecular biology of intervertebral disc degeneration and potential gene therapy strategies for regeneration: a review (2018)

Prasanthi Sampara; Rajkiran Reddy Banala; Satish Kumar Vemuri; Gurava Reddy AVSubbaiah GPV

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-03-23

Description: Understanding the molecular biology of intervertebral disc degeneration and potential gene therapy strategies for regeneration: a review Understanding the molecular biology of intervertebral disc degeneration and potential gene therapy strategies for regeneration: a review, Published online: 22 March 2018; doi:10.1038/s41434-018-0004-0 Understanding the molecular biology of intervertebral disc degeneration and potential gene therapy strategies for regeneration: a review

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

13

Targeted in vivo knock-in of human alpha-1-antitrypsin cDNA using adenoviral delivery of CRISPR/Cas9 (2018)

Calvin J. Stephens; Elena Kashentseva; William Everett; Lyudmila Kaliberova; David T. Curiel

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-03-28

Description: Targeted in vivo knock-in of human alpha-1-antitrypsin cDNA using adenoviral delivery of CRISPR/Cas9 Targeted in vivo knock-in of human alpha-1-antitrypsin cDNA using adenoviral delivery of CRISPR/Cas9, Published online: 27 March 2018; doi:10.1038/s41434-018-0003-1 Targeted in vivo knock-in of human alpha-1-antitrypsin cDNA using adenoviral delivery of CRISPR/Cas9

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

14

Fludarabine and neurotoxicity in engineered T-cell therapy (2018)

Kate L. Lowe; Crystal L. Mackall; Elliot Norry; Rafael Amado; Bent K. Jakobsen; Gwendolyn Binder

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-05-08

Description: Fludarabine and neurotoxicity in engineered T-cell therapy Fludarabine and neurotoxicity in engineered T-cell therapy, Published online: 07 May 2018; doi:10.1038/s41434-018-0019-6 Fludarabine and neurotoxicity in engineered T-cell therapy

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

15

Rationally designed AAV2 and AAVrh8R capsids provide improved transduction in the retina and brain (2018)

Jennifer A. Sullivan; Lisa M. Stanek; Michael J. Lukason; Jie Bu; Shayla R. Osmond; Elizabeth A. Barry; Catherine R. O’Riordan; Lamya S. Shihabuddin; Seng H. Cheng; Abraham Scaria

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-05-23

Description: Rationally designed AAV2 and AAVrh8R capsids provide improved transduction in the retina and brain Rationally designed AAV2 and AAVrh8R capsids provide improved transduction in the retina and brain, Published online: 22 May 2018; doi:10.1038/s41434-018-0017-8 Rationally designed AAV2 and AAVrh8R capsids provide improved transduction in the retina and brain

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

16

Driving cars to the clinic for solid tumors (2018)

Mauro Castellarin; Keisuke Watanabe; Carl H. June; Christopher C. Kloss; Avery D. Posey Jr.

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-06-08

Description: Driving cars to the clinic for solid tumors Driving cars to the clinic for solid tumors, Published online: 07 June 2018; doi:10.1038/s41434-018-0007-x Driving cars to the clinic for solid tumors

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

17

Electroporation-mediated delivery of FER gene enhances innate immune response and improves survival in a murine model of pneumonia (2018)

Vladislav Dolgachev; Sreehari Panicker; Sanjay Balijepalli; Lane Kelly McCandless; Yue Yin; Samantha Swamy; M. V. Suresh; Matthew J. Delano; Mark R. Hemmila; Krishnan Raghavendran; David Machado-Aranda

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-06-16

Description: Electroporation-mediated delivery of FER gene enhances innate immune response and improves survival in a murine model of pneumonia Electroporation-mediated delivery of FER gene enhances innate immune response and improves survival in a murine model of pneumonia, Published online: 15 June 2018; doi:10.1038/s41434-018-0022-y Electroporation-mediated delivery of FER gene enhances innate immune response and improves survival in a murine model of pneumonia

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

18

In vitro evaluation of a lentiviral two-step transcriptional amplification system using GAL4FF transactivator for gene therapy applications in bone repair (2018)

Sofia Bougioukli; Osamu Sugiyama; Ram K. Alluri; Robert Yoho; Daniel A. Oakes; Jay R. Lieberman

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-06-16

Description: In vitro evaluation of a lentiviral two-step transcriptional amplification system using GAL4FF transactivator for gene therapy applications in bone repair In vitro evaluation of a lentiviral two-step transcriptional amplification system using GAL4FF transactivator for gene therapy applications in bone repair, Published online: 15 June 2018; doi:10.1038/s41434-018-0024-9 In vitro evaluation of a lentiviral two-step transcriptional amplification system using GAL4FF transactivator for gene therapy applications in bone repair

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

19

Additive effects of the combined expression of soluble forms of GAS1 and PTEN inhibiting glioblastoma growth (2018)

Laura Sánchez-Hernández; Justino Hernández-Soto; Paula Vergara; Rosa O. González; José Segovia

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-06-26

Description: Additive effects of the combined expression of soluble forms of GAS1 and PTEN inhibiting glioblastoma growth Additive effects of the combined expression of soluble forms of GAS1 and PTEN inhibiting glioblastoma growth, Published online: 25 June 2018; doi:10.1038/s41434-018-0020-0 Additive effects of the combined expression of soluble forms of GAS1 and PTEN inhibiting glioblastoma growth

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

20

CAR-T: trailblazing the path from clinical development to the clinic (2018)

Samuele Butera

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-04-24

Description: CAR-T: trailblazing the path from clinical development to the clinic CAR-T: trailblazing the path from clinical development to the clinic, Published online: 23 April 2018; doi:10.1038/s41434-018-0013-z CAR-T: trailblazing the path from clinical development to the clinic

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

21

LncRNA FTX sponges miR-215 and inhibits phosphorylation of vimentin for promoting colorectal cancer progression (2018)

Yi Yang; Jinpei Zhang; Xi Chen; Xin Xu; Gang Cao; Hua Li; Tao Wu

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-06-21

Description: LncRNA FTX sponges miR-215 and inhibits phosphorylation of vimentin for promoting colorectal cancer progression LncRNA FTX sponges miR-215 and inhibits phosphorylation of vimentin for promoting colorectal cancer progression, Published online: 20 June 2018; doi:10.1038/s41434-018-0026-7 LncRNA FTX sponges miR-215 and inhibits phosphorylation of vimentin for promoting colorectal cancer progression

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

22

Stable and reproducible transgene expression independent of proliferative or differentiated state using BAC TG-EMBED (2018)

Pankaj Chaturvedi; Binhui Zhao; David L. Zimmerman; Andrew S. Belmont

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-06-22

Description: Stable and reproducible transgene expression independent of proliferative or differentiated state using BAC TG-EMBED Stable and reproducible transgene expression independent of proliferative or differentiated state using BAC TG-EMBED, Published online: 21 June 2018; doi:10.1038/s41434-018-0021-z Stable and reproducible transgene expression independent of proliferative or differentiated state using BAC TG-EMBED

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

23

Downreguation of FoxM1 by miR-214 inhibits proliferation and migration in hepatocellular carcinoma (2018)

Chuan Tian; Haixia Wu; Chan Li; Xia Tian; Yong Sun; Enqiang Liu; Xiuyong Liao; Wei Song

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-07-05

Description: Downreguation of FoxM1 by miR-214 inhibits proliferation and migration in hepatocellular carcinoma Downreguation of FoxM1 by miR-214 inhibits proliferation and migration in hepatocellular carcinoma, Published online: 04 July 2018; doi:10.1038/s41434-018-0029-4 Downreguation of FoxM1 by miR-214 inhibits proliferation and migration in hepatocellular carcinoma

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

24

Serotype survey of AAV gene delivery via subconjunctival injection in mice (2018)

Liujiang Song; Telmo Llanga; Laura M. Conatser; Violeta Zaric; Brian C. Gilger; Matthew L. Hirsch

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-08-03

Description: Serotype survey of AAV gene delivery via subconjunctival injection in mice Serotype survey of AAV gene delivery via subconjunctival injection in mice, Published online: 02 August 2018; doi:10.1038/s41434-018-0035-6 Serotype survey of AAV gene delivery via subconjunctival injection in mice

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

25

In vivo delivery of pPERDBY to BALB/c mice by LacVax ® DNA-I and comparison of elicited immune response with conventional immunization methods (2018)

Bhrugu Yagnik; Drashya Sharma; Harish Padh; Priti Desai

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-08-15

Description: In vivo delivery of pPERDBY to BALB/c mice by LacVax ® DNA-I and comparison of elicited immune response with conventional immunization methods In vivo delivery of pPERDBY to BALB/c mice by 〈i〉LacVax〈/i〉〈sup〉®〈/sup〉 〈i〉DNA-I〈/i〉 and comparison of elicited immune response with conventional immunization methods, Published online: 14 August 2018; doi:10.1038/s41434-018-0033-8 In vivo delivery of pPERDBY to BALB/c mice by LacVax ® DNA-I and comparison of elicited immune response with conventional immunization methods

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

26

Nanosphere-mediated co-delivery of VEGF-A and PDGF-B genes for accelerating diabetic foot ulcers healing in rats (2018)

Rongfeng Shi; Weishuai Lian; Shilong Han; Chuanwu Cao; Yinpeng Jin; Yifeng Yuan; Hui Zhao; Maoquan Li

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-06-29

Description: Nanosphere-mediated co-delivery of VEGF-A and PDGF-B genes for accelerating diabetic foot ulcers healing in rats Nanosphere-mediated co-delivery of VEGF-A and PDGF-B genes for accelerating diabetic foot ulcers healing in rats, Published online: 28 June 2018; doi:10.1038/s41434-018-0027-6 Nanosphere-mediated co-delivery of VEGF-A and PDGF-B genes for accelerating diabetic foot ulcers healing in rats

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

27

CAR-T in the clinic: drive with care (2018)

Rafael J. Yáñez-Muñoz; Stephan A. Grupp

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-07-02

Description: CAR-T in the clinic: drive with care CAR-T in the clinic: drive with care, Published online: 01 July 2018; doi:10.1038/s41434-018-0023-x CAR-T in the clinic: drive with care

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

28

More expansive gene transfer to the rat CNS: AAV PHP.EB vector dose–response and comparison to AAV PHP.B (2018)

Robert D. Dayton; Mychal S. Grames; Ronald L. Klein

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-07-17

Description: More expansive gene transfer to the rat CNS: AAV PHP.EB vector dose–response and comparison to AAV PHP.B More expansive gene transfer to the rat CNS: AAV PHP.EB vector dose–response and comparison to AAV PHP.B, Published online: 16 July 2018; doi:10.1038/s41434-018-0028-5 More expansive gene transfer to the rat CNS: AAV PHP.EB vector dose–response and comparison to AAV PHP.B

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

29

Characterization of a replicating expanded tropism oncolytic reovirus carrying the adenovirus E4orf4 gene (2018)

Vera Kemp; Iris J. C. Dautzenberg; Steve J. Cramer; Rob C. Hoeben; Diana J. M. van den Wollenberg

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-07-17

Description: Characterization of a replicating expanded tropism oncolytic reovirus carrying the adenovirus E4orf4 gene Characterization of a replicating expanded tropism oncolytic reovirus carrying the adenovirus E4orf4 gene, Published online: 16 July 2018; doi:10.1038/s41434-018-0032-9 Characterization of a replicating expanded tropism oncolytic reovirus carrying the adenovirus E4orf4 gene

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

30

The murine lung as a factory to produce secreted intrapulmonary and circulatory proteins (2018)

Michael C. Paul-Smith; Kamila M. Pytel; Jean-François Gelinas; Jenny McIntosh; Ian Pringle; Lee Davies; Mario Chan; Cuixiang Meng; Robyn Bell; Lidia Cammack; Caroline Moran; Loren Cameron; Makoto Inoue; Shu Tsugumine; Takashi Hironaka; Deborah R. Gill; Stephen C. Hyde; Amit Nathwani; Eric W. F. W. Alton; Uta Griesenbach

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-07-19

Description: The murine lung as a factory to produce secreted intrapulmonary and circulatory proteins The murine lung as a factory to produce secreted intrapulmonary and circulatory proteins, Published online: 18 July 2018; doi:10.1038/s41434-018-0025-8 The murine lung as a factory to produce secreted intrapulmonary and circulatory proteins

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

31

Correction: Development of an optimized AAV2/5 gene therapy vector for Leber congenital amaurosis owing to defects in RPE65 (2018)

A. Georgiadis; Y. Duran; J. Ribeiro; L. Abelleira-Hervas; S. J. Robbie; B. Sünkel-Laing; S. Fourali; A. Gonzalez-Cordero; E. Cristante; M. Michaelides; J. W. B. Bainbridge; A. J. Smith; R. R. Ali

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-07-26

Description: Correction: Development of an optimized AAV2/5 gene therapy vector for Leber congenital amaurosis owing to defects in RPE65 Correction: Development of an optimized AAV2/5 gene therapy vector for Leber congenital amaurosis owing to defects in RPE65, Published online: 25 July 2018; doi:10.1038/s41434-018-0031-x Correction: Development of an optimized AAV2/5 gene therapy vector for Leber congenital amaurosis owing to defects in RPE65

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

32

Diabetic complication could get a gene therapy boost (2018)

Julio Enrique Castañeda-Delgado

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-08-11

Description: Diabetic complication could get a gene therapy boost Diabetic complication could get a gene therapy boost, Published online: 10 August 2018; doi:10.1038/s41434-018-0037-4 Diabetic complication could get a gene therapy boost

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

33

Metabolically stabilized double-stranded mRNA polyplexes (2018)

Jacob A. Poliskey; Samuel T. Crowley; Raghu Ramanathan; Christopher W. White; Basil Mathew; Kevin G. Rice

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-08-29

Description: Metabolically stabilized double-stranded mRNA polyplexes Metabolically stabilized double-stranded mRNA polyplexes, Published online: 28 August 2018; doi:10.1038/s41434-018-0038-3 Metabolically stabilized double-stranded mRNA polyplexes

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

34

Optimization of viral protein ratios for production of rAAV serotype 5 in the baculovirus system (2018)

Bas Bosma; Francois du Plessis; Erich Ehlert; Bart Nijmeijer; Martin de Haan; Harald Petry; Jacek Lubelski

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-08-02

Description: Optimization of viral protein ratios for production of rAAV serotype 5 in the baculovirus system Optimization of viral protein ratios for production of rAAV serotype 5 in the baculovirus system, Published online: 01 August 2018; doi:10.1038/s41434-018-0034-7 Optimization of viral protein ratios for production of rAAV serotype 5 in the baculovirus system

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

35

Ectopic BAT mUCP-1 overexpression in SKM by delivering a BMP7/PRDM16/PGC-1a gene cocktail or single PRMD16 using non-viral UTMD gene therapy (2018)

Shuyuan Chen; Raul A. Bastarrachea; Jin-Song Shen; Antonio Laviada-Nagel; Ernesto Rodriguez-Ayala; Edna J. Nava-Gonzalez; Pintong Huang; Ralph A. De; Fronzo; Jack W. Kent Jr.Paul A. Grayburn

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-08-03

Description: Ectopic BAT mUCP-1 overexpression in SKM by delivering a BMP7/PRDM16/PGC-1a gene cocktail or single PRMD16 using non-viral UTMD gene therapy Ectopic BAT mUCP-1 overexpression in SKM by delivering a 〈i〉BMP7/PRDM16/PGC-1a〈/i〉 gene cocktail or single 〈i〉PRMD16〈/i〉 using non-viral UTMD gene therapy, Published online: 02 August 2018; doi:10.1038/s41434-018-0036-5 Ectopic BAT mUCP-1 overexpression in SKM by delivering a BMP7/PRDM16/PGC-1a gene cocktail or single PRMD16 using non-viral UTMD gene therapy

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

36

Superior lentiviral vectors designed for BSL-0 environment abolish vector mobilization (2018)

Peirong Hu; Yanmin Bi; Hong Ma; Thipparat Suwanmanee; Brian Zeithaml; Nate J. Fry; Donald B. Kohn; Tal Kafri

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-09-07

Description: Superior lentiviral vectors designed for BSL-0 environment abolish vector mobilization Superior lentiviral vectors designed for BSL-0 environment abolish vector mobilization, Published online: 06 September 2018; doi:10.1038/s41434-018-0039-2 Superior lentiviral vectors designed for BSL-0 environment abolish vector mobilization

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

37

Improved therapeutic potential of MSCs by genetic modification (2018)

Wei Wei; Yong Huang; Dan Li; Hong-Feng Gou; Wei Wang

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-09-26

Description: Improved therapeutic potential of MSCs by genetic modification Improved therapeutic potential of MSCs by genetic modification, Published online: 25 September 2018; doi:10.1038/s41434-018-0041-8 Improved therapeutic potential of MSCs by genetic modification

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

38

Anti-angiogenic treatment of endometriosis via anti-VEGFA siRNA delivery by means of peptide-based carrier in a rat subcutaneous model (2018)

Anna Egorova; Mariya Petrosyan; Marianna Maretina; Natalia Balashova; Lyudmila Polyanskih; Vladislav Baranov; Anton Kiselev

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-09-26

Description: Anti-angiogenic treatment of endometriosis via anti-VEGFA siRNA delivery by means of peptide-based carrier in a rat subcutaneous model Anti-angiogenic treatment of endometriosis via anti-VEGFA siRNA delivery by means of peptide-based carrier in a rat subcutaneous model, Published online: 25 September 2018; doi:10.1038/s41434-018-0042-7 Anti-angiogenic treatment of endometriosis via anti-VEGFA siRNA delivery by means of peptide-based carrier in a rat subcutaneous model

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

39

Scaffold-mediated delivery for non-viral mRNA vaccines (2018)

Ruying Chen; Hong Zhang; Jingxuan Yan; James D. Bryers

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-09-22

Description: Scaffold-mediated delivery for non-viral mRNA vaccines Scaffold-mediated delivery for non-viral mRNA vaccines, Published online: 21 September 2018; doi:10.1038/s41434-018-0040-9 Scaffold-mediated delivery for non-viral mRNA vaccines

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

40

Epistasis between Pax6 Sey and genetic background reinforces the value of defined hybrid mouse models for therapeutic trials (2018)

Jack W. Hickmott; Uvini Gunawardane; Kimberly Jensen; Andrea J. Korecki; Elizabeth M. Simpson

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-09-27

Description: Epistasis between Pax6 Sey and genetic background reinforces the value of defined hybrid mouse models for therapeutic trials Epistasis between 〈i〉Pax6〈/i〉〈sup〉Sey〈/sup〉 and genetic background reinforces the value of defined hybrid mouse models for therapeutic trials, Published online: 26 September 2018; doi:10.1038/s41434-018-0043-6 Epistasis between Pax6 Sey and genetic background reinforces the value of defined hybrid mouse models for therapeutic trials

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

41

Long noncoding RNA Meg3 regulates cardiomyocyte apoptosis in myocardial infarction (2018)

Hongchun Wu; Zhen-Ao Zhao; Junwei Liu; Kaili Hao; You Yu; Xinglong Han; Jingjing Li; Yixuan Wang; Wei Lei; Nianguo Dong; Zhenya Shen; Shijun Hu

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-10-05

Description: Long noncoding RNA Meg3 regulates cardiomyocyte apoptosis in myocardial infarction Long noncoding RNA 〈i〉Meg3〈/i〉 regulates cardiomyocyte apoptosis in myocardial infarction, Published online: 04 October 2018; doi:10.1038/s41434-018-0045-4 Long noncoding RNA Meg3 regulates cardiomyocyte apoptosis in myocardial infarction

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

42

Osteoinduction within BMP-2 transduced muscle tissue fragments with and without a fascia layer: implications for bone tissue engineering (2018)

Bin Ren; Volker M. Betz; Christian Thirion; Michael Salomon; Volkmar Jansson; Peter E. Müller; Oliver B. Betz

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-10-28

Description: Osteoinduction within BMP-2 transduced muscle tissue fragments with and without a fascia layer: implications for bone tissue engineering Osteoinduction within BMP-2 transduced muscle tissue fragments with and without a fascia layer: implications for bone tissue engineering, Published online: 27 October 2018; doi:10.1038/s41434-018-0047-2 Osteoinduction within BMP-2 transduced muscle tissue fragments with and without a fascia layer: implications for bone tissue engineering

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

43

An important step on the long path to clinical application of in utero gene therapy (2018)

Charles Coutelle

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-10-06

Description: An important step on the long path to clinical application of in utero gene therapy An important step on the long path to clinical application of in utero gene therapy, Published online: 05 October 2018; doi:10.1038/s41434-018-0046-3 An important step on the long path to clinical application of in utero gene therapy

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

44

Characterization of abscopal effects of intratumoral electroporation-mediated IL-12 gene therapy (2018)

Anandaroop Mukhopadhyay; Jocelyn Wright; Shawna Shirley; David A. Canton; Christoph Burkart; Richard J. Connolly; Jean S. Campbell; Robert H. Pierce

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-10-16

Description: Characterization of abscopal effects of intratumoral electroporation-mediated IL-12 gene therapy Characterization of abscopal effects of intratumoral electroporation-mediated IL-12 gene therapy, Published online: 15 October 2018; doi:10.1038/s41434-018-0044-5 Characterization of abscopal effects of intratumoral electroporation-mediated IL-12 gene therapy

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

45

Excessive activated T-cell proliferation after anti-CD19 CAR T-cell therapy (2018)

Wen-ying Zhang; Yang Liu; Yao Wang; Jing Nie; Ye-lei Guo; Chun-meng Wang; Han-ren Dai; Qing-ming Yang; Zhi-qiang Wu; Wei-dong Han

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-03-30

Description: Excessive activated T-cell proliferation after anti-CD19 CAR T-cell therapy Excessive activated T-cell proliferation after anti-CD19 CAR T-cell therapy, Published online: 29 March 2018; doi:10.1038/s41434-017-0001-8 Excessive activated T-cell proliferation after anti-CD19 CAR T-cell therapy

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

46

The revving up of CARs (2018)

Muhammad Bilal Abid

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-04-14

Description: The revving up of CARs The revving up of CARs, Published online: 13 April 2018; doi:10.1038/s41434-018-0015-x The revving up of CARs

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

47

Effects of microRNA-292-5p on myocardial ischemia–reperfusion injury through the peroxisome proliferator-activated receptor-α/-γ signaling pathway (2018)

Zhen-Dong Zhu; Ji-Yun Ye; Hua Niu; Yu-Mei Ma; Xue-Mei Fu; Zhong-Hua Xia; Xuan Zhang

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-04-19

Description: Effects of microRNA-292-5p on myocardial ischemia–reperfusion injury through the peroxisome proliferator-activated receptor-α/-γ signaling pathway Effects of microRNA-292-5p on myocardial ischemia–reperfusion injury through the peroxisome proliferator-activated receptor-α/-γ signaling pathway, Published online: 18 April 2018; doi:10.1038/s41434-018-0014-y Effects of microRNA-292-5p on myocardial ischemia–reperfusion injury through the peroxisome proliferator-activated receptor-α/-γ signaling pathway

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

48

Human carbonic anhydrase-8 AAV8 gene therapy inhibits nerve growth factor signaling producing prolonged analgesia and anti-hyperalgesia in mice (2018)

Gerald Z. Zhuang; Udita Upadhyay; Xiaoying Tong; Yuan Kang; Diana M. Erasso; Eugene S. Fu; Konstantinos D. Sarantopoulos; Eden R. Martin; Tim Wiltshire; Luda Diatchenko; Shad B Smith; William Maixner; Roy C. Levitt

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-04-25

Description: Human carbonic anhydrase-8 AAV8 gene therapy inhibits nerve growth factor signaling producing prolonged analgesia and anti-hyperalgesia in mice Human carbonic anhydrase-8 AAV8 gene therapy inhibits nerve growth factor signaling producing prolonged analgesia and anti-hyperalgesia in mice, Published online: 24 April 2018; doi:10.1038/s41434-018-0018-7 Human carbonic anhydrase-8 AAV8 gene therapy inhibits nerve growth factor signaling producing prolonged analgesia and anti-hyperalgesia in mice

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

49

Effect of PAK1 gene silencing on proliferation and apoptosis in hepatocellular carcinoma cell lines MHCC97-H and HepG2 and cells in xenograft tumor (2018)

Zhi-Lei Zhang; Guang-chao Liu; Li Peng; Chong Zhang; Yu-Ming Jia; Wu-Han Yang; Lei Mao

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2018-05-26

Description: Effect of PAK1 gene silencing on proliferation and apoptosis in hepatocellular carcinoma cell lines MHCC97-H and HepG2 and cells in xenograft tumor Effect of PAK1 gene silencing on proliferation and apoptosis in hepatocellular carcinoma cell lines MHCC97-H and HepG2 and cells in xenograft tumor, Published online: 25 May 2018; doi:10.1038/s41434-018-0016-9 Effect of PAK1 gene silencing on proliferation and apoptosis in hepatocellular carcinoma cell lines MHCC97-H and HepG2 and cells in xenograft tumor

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

50

Antigen-presenting cell-targeted lentiviral vectors do not support the development of productive T-cell effector responses: implications for in vivo targeted vaccine delivery (2017)

C Goyvaerts; Y De Vlaeminck; D Escors; S Lienenklaus; M Keyaerts; G Raes; K Breckpot

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-06-16

Description: Antigen-presenting cell-targeted lentiviral vectors do not support the development of productive T-cell effector responses: implications for in vivo targeted vaccine delivery Gene Therapy 24, 370 (June 2017). doi:10.1038/gt.2017.30 Authors: C Goyvaerts, Y De Vlaeminck, D Escors, S Lienenklaus, M Keyaerts, G Raes & K Breckpot

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

51

Delivering efficient liver-directed AAV-mediated gene therapy (2017)

J Baruteau; S N Waddington; I E Alexander; P Gissen

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-05-20

Description: Delivering efficient liver-directed AAV-mediated gene therapy Gene Therapy 24, 263 (May 2017). doi:10.1038/gt.2016.90 Authors: J Baruteau, S N Waddington, I E Alexander & P Gissen

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

52

Live-cell imaging to compare the transfection and gene silencing efficiency of calcium phosphate nanoparticles and a liposomal transfection agent (2017)

S Chernousova; M Epple

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-05-20

Description: Live-cell imaging to compare the transfection and gene silencing efficiency of calcium phosphate nanoparticles and a liposomal transfection agent Gene Therapy 24, 282 (May 2017). doi:10.1038/gt.2017.13 Authors: S Chernousova & M Epple

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

53

Detailed comparison of retroviral vectors and promoter configurations for stable and high transgene expression in human induced pluripotent stem cells (2017)

D Hoffmann; J W Schott; F K Geis; L Lange; F-J Müller; D Lenz; D Zychlinski; D Steinemann; M Morgan; T Moritz; A Schambach

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-05-20

Description: Detailed comparison of retroviral vectors and promoter configurations for stable and high transgene expression in human induced pluripotent stem cells Gene Therapy 24, 298 (May 2017). doi:10.1038/gt.2017.20 Authors: D Hoffmann, J W Schott, F K Geis, L Lange, F-J Müller, D Lenz, D Zychlinski, D Steinemann, M Morgan, T Moritz & A Schambach

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

54

Efficient CNS targeting in adult mice by intrathecal infusion of single-stranded AAV9-GFP for gene therapy of neurological disorders (2017)

K Bey; C Ciron; L Dubreil; J Deniaud; M Ledevin; J Cristini; V Blouin; P Aubourg; M-A Colle

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-05-20

Description: Efficient CNS targeting in adult mice by intrathecal infusion of single-stranded AAV9-GFP for gene therapy of neurological disorders Gene Therapy 24, 325 (May 2017). doi:10.1038/gt.2017.18 Authors: K Bey, C Ciron, L Dubreil, J Deniaud, M Ledevin, J Cristini, V Blouin, P Aubourg & M-A Colle

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

55

Gene Therapy, more than ever—a new vision for the journal (2017)

R J Yáñez-Muñoz

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-09-30

Description: Gene Therapy, more than ever—a new vision for the journal Gene Therapy 24, 493 (September 2017). doi:10.1038/gt.2017.60 Author: R J Yáñez-Muñoz

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

56

Spinraza—a rare disease success story (2017)

V Prakash

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-09-30

Description: Spinraza—a rare disease success story Gene Therapy 24, 497 (September 2017). doi:10.1038/gt.2017.59 Author: V Prakash

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

57

Therapeutic approaches for spinal muscular atrophy (SMA) (2017)

M Scoto; R S Finkel; E Mercuri; F Muntoni

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-09-30

Description: Therapeutic approaches for spinal muscular atrophy (SMA) Gene Therapy 24, 514 (September 2017). doi:10.1038/gt.2017.45 Authors: M Scoto, R S Finkel, E Mercuri & F Muntoni

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

58

How the discovery of ISS-N1 led to the first medical therapy for spinal muscular atrophy (2017)

N N Singh; M D Howell; E J Androphy; R N Singh

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-09-30

Description: How the discovery of ISS-N1 led to the first medical therapy for spinal muscular atrophy Gene Therapy 24, 520 (September 2017). doi:10.1038/gt.2017.34 Authors: N N Singh, M D Howell, E J Androphy & R N Singh

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

59

Will rising prices and budget constraints prevent patients from accessing novel gene therapies? (2017)

A Kent; J Spink

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-09-30

Description: Will rising prices and budget constraints prevent patients from accessing novel gene therapies? Gene Therapy 24, 542 (September 2017). doi:10.1038/gt.2017.66 Authors: A Kent & J Spink

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

60

New treatments for serious conditions: ethical implications (2017)

N M P King; C E Bishop

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-09-30

Description: New treatments for serious conditions: ethical implications Gene Therapy 24, 534 (September 2017). doi:10.1038/gt.2017.32 Authors: N M P King & C E Bishop

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

61

The importance of international collaboration for rare diseases research: a European perspective (2017)

D Julkowska; C P Austin; C M Cutillo; D Gancberg; C Hager; J Halftermeyer; A H Jonker; L P L Lau; I Norstedt; A Rath; R Schuster; E Simelyte; S van Weely

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-09-30

Description: The importance of international collaboration for rare diseases research: a European perspective Gene Therapy 24, 562 (September 2017). doi:10.1038/gt.2017.29 Authors: D Julkowska, C P Austin, C M Cutillo, D Gancberg, C Hager, J Halftermeyer, A H Jonker, L P L Lau, I Norstedt, A Rath, R Schuster, E Simelyte & S van Weely

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

62

The SMA Trust: the role of a disease-focused research charity in developing treatments for SMA (2017)

V Christie-Brown; J Mitchell; K Talbot

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-09-30

Description: The SMA Trust: the role of a disease-focused research charity in developing treatments for SMA Gene Therapy 24, 544 (September 2017). doi:10.1038/gt.2017.47 Authors: V Christie-Brown, J Mitchell & K Talbot

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

63

The state of gene therapy research in Africa, its significance and implications for the future (2017)

P Arbuthnot; M B Maepa; A Ely; M S Pepper

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-09-30

Description: The state of gene therapy research in Africa, its significance and implications for the future Gene Therapy 24, 581 (September 2017). doi:10.1038/gt.2017.57 Authors: P Arbuthnot, M B Maepa, A Ely & M S Pepper

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

64

Management of neuromuscular diseases and spinal muscular atrophy in Latin America (2017)

S Monges; A L Rosa

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-09-30

Description: Management of neuromuscular diseases and spinal muscular atrophy in Latin America Gene Therapy 24, 578 (September 2017). doi:10.1038/gt.2017.68 Authors: S Monges & A L Rosa

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

65

An AAVrh10-CAG-CYP21-HA vector allows persistent correction of 21-hydroxylase deficiency in a Cyp21−/− mouse model (2017)

M Perdomini; C Dos Santos; C Goumeaux; V Blouin; P Bougnères

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-05-20

Description: An AAVrh10-CAG-CYP21-HA vector allows persistent correction of 21-hydroxylase deficiency in a Cyp21−/− mouse model Gene Therapy 24, 275 (May 2017). doi:10.1038/gt.2017.10 Authors: M Perdomini, C Dos Santos, C Goumeaux, V Blouin & P Bougnères

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

66

MnSOD mediated by HSV vectors in the periaqueductal gray suppresses morphine withdrawal in rats (2017)

T Iida; H Yi; S Liu; D Ikegami; W Zheng; Q Liu; K Takahashi; Y Kashiwagi; W F Goins; J C Glorioso; S Hao

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-05-20

Description: MnSOD mediated by HSV vectors in the periaqueductal gray suppresses morphine withdrawal in rats Gene Therapy 24, 314 (May 2017). doi:10.1038/gt.2017.22 Authors: T Iida, H Yi, S Liu, D Ikegami, W Zheng, Q Liu, K Takahashi, Y Kashiwagi, W F Goins, J C Glorioso & S Hao

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

67

AAV9-mediated engineering of autotransplanted kidney of non-human primates (2017)

S Tomasoni; P Trionfini; N Azzollini; L Zentilin; M Giacca; S Aiello; L Longaretti; E Cozzi; N Baldan; G Remuzzi; A Benigni

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-05-20

Description: AAV9-mediated engineering of autotransplanted kidney of non-human primates Gene Therapy 24, 308 (May 2017). doi:10.1038/gt.2017.21 Authors: S Tomasoni, P Trionfini, N Azzollini, L Zentilin, M Giacca, S Aiello, L Longaretti, E Cozzi, N Baldan, G Remuzzi & A Benigni

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

68

Gene therapy research in Asia (2017)

H-X Deng; Y Wang; Q-r Ding; D-l Li; Yu-quan Wei

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-09-30

Description: Gene therapy research in Asia Gene Therapy 24, 572 (September 2017). doi:10.1038/gt.2017.62 Authors: H-X Deng, Y Wang, Q-r Ding, D-l Li & Yu-quan Wei

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

69

Developing gene and cell therapies for rare diseases: an opportunity for synergy between academia and industry (2017)

F Mavilio

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-09-30

Description: Developing gene and cell therapies for rare diseases: an opportunity for synergy between academia and industry Gene Therapy 24, 590 (September 2017). doi:10.1038/gt.2017.36 Author: F Mavilio

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

70

Compilation of online resources of relevance to ‘Spinraza and advanced therapies: a stakeholder special’ issue of Gene Therapy (2017)

V Prakash; R J Yáñez-Muñoz

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-09-30

Description: Compilation of online resources of relevance to ‘Spinraza and advanced therapies: a stakeholder special’ issue of Gene Therapy Gene Therapy 24, 599 (September 2017). doi:10.1038/gt.2017.61 Authors: V Prakash & R J Yáñez-Muñoz

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

71

Delivering advanced therapies: the big pharma approach (2017)

J Tarnowski; D Krishna; L Jespers; A Ketkar; R Haddock; J Imrie; S Kili

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-09-30

Description: Delivering advanced therapies: the big pharma approach Gene Therapy 24, 593 (September 2017). doi:10.1038/gt.2017.65 Authors: J Tarnowski, D Krishna, L Jespers, A Ketkar, R Haddock, J Imrie & S Kili

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

72

Effects of herpes simplex virus vectors encoding poreless TRPV1 or protein phosphatase 1α in a rat cystitis model induced by hydrogen peroxide (2017)

S Takai; T Majima; B Reinhart; W F Goins; Y Funahashi; M Gotoh; P Tyagi; J C Glorioso; N Yoshimura

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-10-26

Description: Effects of herpes simplex virus vectors encoding poreless TRPV1 or protein phosphatase 1α in a rat cystitis model induced by hydrogen peroxide Gene Therapy, Published online: 20 October 2017; doi:10.1038/gt.2017.94

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

73

Optimization of lentiviral vector production for scale-up in fixed-bed bioreactor (2017)

A J Valkama; H M Leinonen; E M Lipponen; V Turkki; J Malinen; T Heikura; S Ylä-Herttuala; H P Lesch

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-10-26

Description: Optimization of lentiviral vector production for scale-up in fixed-bed bioreactor Gene Therapy, Published online: 5 October 2017; doi:10.1038/gt.2017.91

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

74

Management of neuromuscular diseases and spinal muscular atrophy in Latin America (2017)

S Monges; A L Rosa

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-10-26

Description: Management of neuromuscular diseases and spinal muscular atrophy in Latin America Gene Therapy, Published online: 28 September 2017; doi:10.1038/gt.2017.68

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

75

Site-directed RNA editing by adenosine deaminase acting on RNA (ADAR1) for correction of the genetic code in gene therapy (2017)

T A Azad; S Bhakta; T Tsukahara

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-10-26

Description: Site-directed RNA editing by adenosine deaminase acting on RNA (ADAR1) for correction of the genetic code in gene therapy Gene Therapy, Published online: 6 October 2017; doi:10.1038/gt.2017.90

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

76

Gene therapy—from small beginnings to where we are now (2017)

J C Glorioso; N Lemoine

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-10-26

Description: Gene therapy—from small beginnings to where we are now Gene Therapy, Published online: 28 September 2017; doi:10.1038/gt.2017.23

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

77

Gene Therapy , more than ever—a new vision for the journal (2017)

R J Yáñez-Muñoz

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-10-26

Description: Gene Therapy , more than ever—a new vision for the journal Gene Therapy, Published online: 28 September 2017; doi:10.1038/gt.2017.60

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

78

Spinraza—a rare disease success story (2017)

V Prakash

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-10-26

Description: Spinraza—a rare disease success story Gene Therapy, Published online: 28 September 2017; doi:10.1038/gt.2017.59

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

79

Compilation of online resources of relevance to ‘Spinraza and advanced therapies: a stakeholder special’ issue of Gene Therapy (2017)

V Prakash; R J Yáñez-Muñoz

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-10-26

Description: Compilation of online resources of relevance to ‘Spinraza and advanced therapies: a stakeholder special’ issue of Gene Therapy Gene Therapy, Published online: 28 September 2017; doi:10.1038/gt.2017.61

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

80

Minority report: targeting emerging viruses before their emergence (2017)

B D Greenbaum; N Vabret

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-12-01

Description: Minority report: targeting emerging viruses before their emergence Minority report: targeting emerging viruses before their emergence, Published online: 30 November 2017; doi:10.1038/gt.2017.93 Minority report: targeting emerging viruses before their emergence

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink

Signatur	Availability

Others were also interested in ...

PAPER CURRENT

Fulltext

81

Strategy to detect pre-existing immunity to AAV gene therapy (2017)

L Falese; K Sandza; B Yates; S Triffault; S Gangar; B Long; L Tsuruda; B Carter; C Vettermann; S J Zoog; S Fong

Nature Publishing Group

In: Gene Therapy

add to mindlist on the mindlist

Details

Publication Date: 2017-11-07

Description: Strategy to detect pre-existing immunity to AAV gene therapy Strategy to detect pre-existing immunity to AAV gene therapy, Published online: 06 November 2017; doi:10.1038/gt.2017.95

Print ISSN: 0969-7128

Electronic ISSN: 1476-5462

Topics: Biology , Medicine

Published by Nature Publishing Group

Permalink